siRNA screen identifies QPCT as a druggable target for Huntington's disease.
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Authors
Lam, Wun
Hannus, Michael
Sönnichsen, Birte
Imarisio, Sara
Tarditi, Alessia
Menzies, Fiona
Dami, Teresa Ed
Gonzalez-Couto, Eduardo
Lazzeroni, Giulia
Heitz, Freddy
Diamanti, Daniela
Massai, Luisa
Marconi, Guido
Caramelli, Chiara
Nencini, Arianna
Andreini, Matteo
Sardone, Gian Luca
Caradonna, Nicola P
Porcari, Valentina
Scali, Carla
Schneider, Reinhard
Pollio, Giuseppe
Caricasole, Andrea
Publication Date
2015-05Journal Title
Nature chemical biology
ISSN
1552-4450
Volume
11
Issue
5
Pages
347-354
Language
eng
Type
Article
This Version
AM
Physical Medium
Print-Electronic
Metadata
Show full item recordCitation
Jimenez-Sanchez, M., Lam, W., Hannus, M., Sönnichsen, B., Imarisio, S., Fleming, A., Tarditi, A., et al. (2015). siRNA screen identifies QPCT as a druggable target for Huntington's disease.. Nature chemical biology, 11 (5), 347-354. https://doi.org/10.1038/nchembio.1790
Keywords
Neurons, Cells, Cultured, Animals, Mice, Inbred C57BL, Zebrafish, Humans, Mice, Drosophila, Huntington Disease, Aminoacyltransferases, alpha-Crystallin B Chain, Green Fluorescent Proteins, Nerve Tissue Proteins, RNA, Small Interfering, Enzyme Inhibitors, Drug Evaluation, Preclinical, Computational Biology, Mutation, Huntingtin Protein
Sponsorship
Wellcome Trust (095317/Z/11/Z)
MRC (MR/J006904/1)
Wellcome Trust (100140/Z/12/Z)
Wellcome Trust (095317/Z/11/A)
EC FP7 CP (305121)
Identifiers
External DOI: https://doi.org/10.1038/nchembio.1790
This record's URL: https://www.repository.cam.ac.uk/handle/1810/270483
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