CRISPR-Cas9 correction of <i>OPA1</i> c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs.

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Authors

Sladen, Paul E

Perdigão, Pedro RL

Salsbury, Grace

Novoselova, Tatiana

van der Spuy, Jacqueline

Chapple, J Paul

  Yu Wai Man, Patrick

Cheetham, Michael E

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Publication Date

2021-12

Journal Title

Molecular therapy. Nucleic acids

ISSN

2162-2531

Volume

26

Pages

432-443

Language

eng

Type

Article

This Version

VoR

Physical Medium

Electronic-eCollection

Metadata

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Citation

Sladen, P. E., Perdigão, P. R., Salsbury, G., Novoselova, T., van der Spuy, J., Chapple, J. P., Yu Wai Man, P., & et al. (2021). CRISPR-Cas9 correction of <i>OPA1</i> c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs.. Molecular therapy. Nucleic acids, 26 432-443. https://doi.org/10.1016/j.omtn.2021.08.015

Identifiers

External DOI: https://doi.org/10.1016/j.omtn.2021.08.015

This record's URL: https://www.repository.cam.ac.uk/handle/1810/330150



Rights

Attribution 4.0 International

Licence URL: https://creativecommons.org/licenses/by/4.0/